Drug for rare disease brings 'joy and hope'

A teenager in Europe becomes the first to benefit from leniolisib, a new drug offering hope for APDS, a rare immune disorder. Mary Catchpole, 19, whose family has been affected by the condition, expressed joy at the newfound treatment. Leniolisib is the first targeted therapy for APDS, blocking the enzyme causing immune system abnormalities, potentially transforming the lives of those with the disorder.